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Non-viral mediated gene transfer of porphobilinogen deaminase into mammalian cells

Author
JOHANSSON, A1 ; MÖLLER, C2 ; GELLERFORS, P2 ; HARPER, P1
[1] Porphyria Centre Sweden, Department of Medical Laboratory Sciences and Technology, Division of Clinical Chemistry, Karolinska Institute, Huddinge University Hospital, Stockholm, Sweden
[2] HemeBiotech A/S, Lidingö, Sweden
Source

Scandinavian journal of clinical & laboratory investigation. 2002, Vol 62, Num 2, pp 105-113 ; ref : 30 ref

CODEN
SJCLAY
ISSN
0036-5513
Scientific domain
Medical laboratory techniques
Publisher
Scandinavian University Press, Oslo
Publication country
Norway
Document type
Article
Language
English
Keyword (fr)
Aigu DNA Fibroblaste Homme Hydroxymethylbilane synthase Intermittent Lignée HeLa Lignée cellulaire établie Plasmide Porphyrie Porphyrine Thérapie génique Traitement Transfection Transfert génétique EC 4.3.1.8 Ammonia-lyases Appareil digestif pathologie Carbon-nitrogen lyases Enzyme Lyases Maladie héréditaire Métabolisme pathologie Photosensibilité Système nerveux pathologie
Keyword (en)
Acute DNA Fibroblast Human Hydroxymethylbilane synthase Intermittent Hela cell line Established cell line Plasmid Porphyria Porphyrin Gene therapy Treatment Transfection Genetic transfer EC 4.3.1.8 Ammonia-lyases Digestive diseases Carbon-nitrogen lyases Enzyme Lyases Genetic disease Metabolic diseases Photosensitivity Nervous system diseases
Keyword (es)
Agudo DNA Fibroblasto Hombre Hydroxymethylbilane synthase Intermitente Célula HeLa Línea celular establecida Plasmido Porfiria Porfirina Terapia génica Tratamiento Transfección Transferencia genética Ammonia-lyases Aparato digestivo patología Carbon-nitrogen lyases Enzima Lyases Enfermedad hereditaria Metabolismo patología Fotosensibilidad Sistema nervioso patología
Classification
Pascal
002 Biological and medical sciences / 002B Medical sciences / 002B22 Metabolic diseases / 002B22E Other metabolic disorders / 002B22E02 Pigments (porphyrias, hyperbilirubinemias...)

Discipline
Metabolic diseases
Origin
Inist-CNRS
Database
PASCAL
INIST identifier
13741538

Sauf mention contraire ci-dessus, le contenu de cette notice bibliographique peut être utilisé dans le cadre d’une licence CC BY 4.0 Inist-CNRS / Unless otherwise stated above, the content of this bibliographic record may be used under a CC BY 4.0 licence by Inist-CNRS / A menos que se haya señalado antes, el contenido de este registro bibliográfico puede ser utilizado al amparo de una licencia CC BY 4.0 Inist-CNRS

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