Characterization of a Recombinant Adeno-Associated Virus Type 2 Reference Standard Material

Autor

LOCK, Martin¹ ; MCGORRAY, Susan² ; CHIORINI, John A¹¹ ; CHTARTO, Abdelwahed^{12 13} ; CLARK, K. Reed^{14 15} ; CONLON, Thomas¹⁰ ; DARMON, Christophe⁷ ; DORIA, Monica⁴ ; DOUAR, Anne¹⁶ ; FLOTTE, Terence R^{17 18} ; FRANCIS, Joyce D⁸ ; FRANCOIS, Achille⁷ ; AURICCHIO, Alberto^{3 4} ; GIACCA, Mauro¹⁹ ; KORN, Michael T¹ ; KORYTOV, Irina¹⁰ ; LEON, Xavier⁵ ; LEUCHS, Barbara²⁰ ; LUX, Gabriele²¹ ; MELAS, Catherine^{12 13} ; MIZUKAMI, Hiroaki²² ; MOULLIER, Philippe⁷ ; MÜLLER, Marcus²⁰ ; AYUSO, Eduard⁵ ; OZAWA, Keiya²² ; PHILIPSBERG, Tina¹⁰ ; POULARD, Karine¹⁶ ; RAUPP, Christina²⁰ ; RIVIERE, Christel¹⁶ ; ROOSENDAAL, Sigrid D²³ ; SAMULSKI, R. Jude⁶ ; SOLTYS, Steven M⁶ ; SUROSKY, Richard²⁴ ; TENENBAUM, Liliane^{12 13} ; BEECHAM, E. Jeffrey⁶ ; THOMAS, Darby L²⁵ ; VAN MONTFORT, Bart²³ ; VERES, Gabor²⁵ ; WRIGHT, J. Fraser; YILI XU²⁴ ; ZELENAIA, Olga; ZENTILIN, Lorena¹⁹ ; SNYDER, Richard O^{8 9} ; BLOUIN-TAVEL, Véronique⁷ ; BOSCH, Fatima⁵ ; BOSE, Mahuya⁸ ; BYRNE, Barry J^{10 9} ; CATON, Tina⁸
[1] Gene Therapy Program, Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA 19104, United States
[2] Department of Epidemiology and Health Policy Research, University of Florida College of Medicine, Gainesville, FL 32610, United States
[3] Medical Genetics, Department of Pediatrics, Federico II University, 80131 Naples, Italy
[4] Telethon Institute of Genetics and Medicine (TIGEM), 80131 Naples, Italy
[5] Center of Animal Biotechnology and Gene Therapy and Department of Biochemistry and Molecular Biology, School of Veterinary Medicine, Universitat Autònoma de Barcelona, 08193-Bellaterra, Spain
[6] Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, United States
[7] INSERM UMR649, Centre Hospitalier Universitaire de Nantes, 44007 Nantes, France
[8] Center of Excellence for Regenerative Health Biotechnology, University of Florida, Gainesville, FL 32611, United States
[9] Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL 32610, United States
[10] Powell Gene Therapy Center Vector Core, University of Florida, Gainesville, FL 32611, United States
[11] Molecular Physiology and Therapeutics Branch, National Institute of Dental and Craniofacial Research, National Institutes of Health, Bethesda, MD 20892, United States
[12] Laboratory of Experimental Neurosurgery, Free University of Brussels, 1070 Brussels, Belgium
[13] Multidisciplinary Research Institute, Free University of Brussels, 1070 Brussels, Belgium
[14] Center for Gene Therapy, Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, United States
[15] Department of Pediatrics, Ohio State University, Columbus, OH 43210, United States
[16] Généthon, 91000 Evry, France
[17] Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01655, United States
[18] Department of Pediatrics, University of Massachusetts Medical School, Worcester, MA 01655, United States
[19] Molecular Medicine Laboratory, International Center for Genetic Engineering and Biotechnology (ICGEB), 34149 Trieste, Italy
[20] Infection and Cancer Program, German Cancer Research Center, 69120 Heidelberg, Germany
[21] Pharmazeutische Fabrik Dr. Reckeweg, 64625 Bensheim, Germany
[22] Division of Genetic Therapeutics, Center for Molecular Medicine, Jichi Medical University, Shimotsuke 329-0498, Japan
[23] Amsterdam Molecular Therapeutics, 1100 Amsterdam, Netherlands
[24] Sangamo BioSciences, Richmond, CA 94804, United States
[25] Applied Genetic Technologies, Alachua, FL 32615, United States

Fuente

Human gene therapy. 2010, Vol 21, Num 10, pp 1273-1285, 13 p ; ref : 3/4 p

CODEN

HGTHE3

ISSN

1043-0342

Campo Científico

Genetics

Editor

Liebert, Larchmont, NY

País de la publicación

United States

Tipo de documento

Article

Idioma

English

Palabra clave (fr)

Caractérisation Dependovirus Etalon Thérapie génique Virus recombinant Parvoviridae Parvovirinae Virus

Palabra clave (in)

Characterization Dependovirus Standard Gene therapy Recombinant virus Parvoviridae Parvovirinae Virus

Palabra clave (es)

Caracterización Dependovirus Marco Terapia génica Virus recombinante Parvoviridae Parvovirinae Virus

Clasificación

Pascal

002 Biological and medical sciences / 002A Fundamental and applied biological sciences. Psychology / 002A31 Biotechnology / 002A31D Industrial applications and implications. Economical aspects / 002A31D01 Health. Pharmaceutical industry / 002A31D01D Gene therapy

Pascal

002 Biological and medical sciences / 002B Medical sciences / 002B27 Anesthesia. Intensive care medicine. Transfusions. Cell therapy and gene therapy / 002B27D Transfusions. Complications. Transfusion reactions. Cell and gene therapy / 002B27D03 Applied cell therapy and gene therapy

Disciplina

Anaesthesia. Reanimation. Transfusion. Cell therapy and gene therapy Biotechnology

Procedencia

Inist-CNRS

Base de datos

PASCAL

Identificador INIST

23341273

Sauf mention contraire ci-dessus, le contenu de cette notice bibliographique peut être utilisé dans le cadre d’une licence CC BY 4.0 Inist-CNRS / Unless otherwise stated above, the content of this bibliographic record may be used under a CC BY 4.0 licence by Inist-CNRS / A menos que se haya señalado antes, el contenido de este registro bibliográfico puede ser utilizado al amparo de una licencia CC BY 4.0 Inist-CNRS