Availability of and Access to Orphan Drugs: An International Comparison of Pharmaceutical Treatments for Pulmonary Arterial Hypertension, Fabry Disease, Hereditary Angioedema and Chronic Myeloid Leukaemia
- Author
- BLANKART, Carl Rudolf1 2 ; STARGARDT, Tom1 2 ; SCHREYÖGG, Jonas1 2
[1] Institute of Health Economics and Health Care Management, Helmholtz Zentrum München, German Research Center for Environmental Health, Munich, Germany
[2] Institute for Health Care Management and Health Economics, School of Business, Economics and Social Sciences, University of Hamburg, Hamburg, Germany - Source
PharmacoEconomics (Auckland). 2011, Vol 29, Num 1, pp 63-82, 20 p ; ref : 48 ref
- ISSN
- 1170-7690
- Scientific domain
- Hygiene and public health, epidemiology, occupational medicine; Pharmacology drugs
- Publisher
- Adis International, Auckland
- Publication country
- New Zealand
- Document type
- Article
- Language
- English
- Keyword (fr)
- Accessibilité Artériopathie Coût Economie santé Etude comparative Homme Hypertension artérielle pulmonaire Héréditaire International Leucémie myéloïde chronique Lipide Médicament orphelin Oedème angioneurotique Pathologie des artères Santé publique Sphingolipidose héréditaire de Fabry Traitement Allergie Cancer Enzymopathie Hémopathie maligne Immunopathologie Lipoïdose Maladie héréditaire Maladie métabolique Pathologie de l'appareil circulatoire Pathologie de l'appareil respiratoire Pathologie de la peau Pathologie des vaisseaux sanguins Pathologie du système nerveux Syndrome myéloprolifératif
- Keyword (en)
- Accessibility Arteriopathy Costs Health economy Comparative study Human Pulmonary hypertension Hereditary International Chronic myelogenous leukemia Lipids Orphan drug Angioneurotic edema Arterial disease Public health Fabry disease Treatment Allergy Cancer Enzymopathy Malignant hemopathy Immunopathology Lipoidosis Genetic disease Metabolic diseases Cardiovascular disease Respiratory disease Skin disease Vascular disease Nervous system diseases Myeloproliferative syndrome
- Keyword (es)
- Accesibilidad Arteriopatía Coste Economía salud Estudio comparativo Hombre Hipertensión arterial pulmonar Hereditario Internacional Leucemia mieloidea crónica Lípido Medicamento huérfano Edema angioneurótico Arteria patología Salud pública Esfingolipidosis hereditaria Fabry Tratamiento Alergia Cáncer Enzimopatía Hemopatía maligna Inmunopatología Lipoidosis Enfermedad hereditaria Metabolismo patología Aparato circulatorio patología Aparato respiratorio patología Piel patología Vaso sanguíneo patología Sistema nervioso patología Mieloproliferativo síndrome
- Classification
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B02 Pharmacology. Drug treatments / 002B02W Miscellaneous
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B11 Pneumology / 002B11C Pulmonary hypertension. Acute cor pulmonale. Pulmonary embolism. Pulmonary vascular diseases
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B12 Cardiology. Vascular system / 002B12B Blood and lymphatic vessels / 002B12B03 Diseases of the peripheral vessels. Diseases of the vena cava. Miscellaneous
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B22 Metabolic diseases / 002B22D Errors of metabolism / 002B22D02 Lipids (lysosomal enzyme disorders, storage diseases)
- Discipline
- Cardiology. Circulatory system General pharmacology Metabolic diseases Pulmonology
- Origin
- Inist-CNRS
- Database
- PASCAL
- INIST identifier
- 23918999
Sauf mention contraire ci-dessus, le contenu de cette notice bibliographique peut être utilisé dans le cadre d’une licence CC BY 4.0 Inist-CNRS / Unless otherwise stated above, the content of this bibliographic record may be used under a CC BY 4.0 licence by Inist-CNRS / A menos que se haya señalado antes, el contenido de este registro bibliográfico puede ser utilizado al amparo de una licencia CC BY 4.0 Inist-CNRS
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