Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges : Gene-based therapies
- Author
- MINGOZZI, Federico1 ; HIGH, Katherine A1 2 3
[1] Center for Cellular and Molecular Therapeutics, The Children's Hospital of Philadelphia, United States
[2] Howard Hughes Medical Institute, The Children's Hospital of Philadelphia, 3501 Civic Center Boulevard, 5thFloor CTRB, Philadelphia, Pennsylvania 19104, United States
[3] University of Pennsylvania School of Medicine, 3600 Market Street, Suite 240, Philadelphia, Pennsylvania 19104-2646, United States - Source
Nature reviews. Genetics (Print). 2011, Vol 12, Num 5, pp 341-355, 15 p ; ref : 176 ref
- Publisher
- Nature Publishing Group, London
- Publication country
- United Kingdom
- Document type
- Article
- Language
- English
- Keyword (fr)
- Article synthèse Dependovirus In vivo Maladie héréditaire Thérapie génique Transfert génétique Vecteur Parvoviridae Parvovirinae Virus
- Keyword (en)
- Review Dependovirus In vivo Genetic disease Gene therapy Genetic transfer Vector Parvoviridae Parvovirinae Virus
- Keyword (es)
- Artículo síntesis Dependovirus In vivo Enfermedad hereditaria Terapia génica Transferencia genética Vector Parvoviridae Parvovirinae Virus
- Classification
- Pascal
- 002 Biological and medical sciences / 002A Fundamental and applied biological sciences. Psychology / 002A07 Genetics of eukaryotes. Biological and molecular evolution
- Pascal
- 002 Biological and medical sciences / 002A Fundamental and applied biological sciences. Psychology / 002A31 Biotechnology / 002A31D Industrial applications and implications. Economical aspects / 002A31D01 Health. Pharmaceutical industry / 002A31D01D Gene therapy
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B27 Anesthesia. Intensive care medicine. Transfusions. Cell therapy and gene therapy / 002B27D Transfusions. Complications. Transfusion reactions. Cell and gene therapy / 002B27D03 Applied cell therapy and gene therapy
- Discipline
- Anaesthesia. Reanimation. Transfusion. Cell therapy and gene therapy Biotechnology Eukaryotes genetics. Biological and molecular evolution
- Origin
- Inist-CNRS
- Database
- PASCAL
- INIST identifier
- 24069373
Sauf mention contraire ci-dessus, le contenu de cette notice bibliographique peut être utilisé dans le cadre d’une licence CC BY 4.0 Inist-CNRS / Unless otherwise stated above, the content of this bibliographic record may be used under a CC BY 4.0 licence by Inist-CNRS / A menos que se haya señalado antes, el contenido de este registro bibliográfico puede ser utilizado al amparo de una licencia CC BY 4.0 Inist-CNRS
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DOI
10.1038/nrg2988 
https://dx.doi.org/10.1038/nrg2988
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