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A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency

Author
HACEIN-BEY-ABINA, S1 4 5 6 ; PAI, S.-Y11 13 14 ; CACCAVELLI, L1 4 7 8 ; CROS, G2 ; DE OLIVEIRA, S23 ; FERNANDEZ, K. S25 ; GUO, D11 13 ; HARRIS, C. E11 ; HOPKINS, G11 ; LEHMANN, L. E11 13 14 ; LIM, A9 ; LONDON, W. B11 13 14 ; GASPAR, H. B11 18 19 ; VAN DER LOO, J. C. M22 ; MALANI, N; MALE, F; MALIK, P22 ; MARINOVIC, M. A; McNICOL, A.-M19 ; MOSHOUS, D2 7 ; NEVEN, B2 7 ; OLEASTRO, M; PICARD, C2 3 7 ; ARMANT, M14 15 ; RITZ, J14 15 16 19 ; RIVAT, C; SCHAMBACH, A; SHAW, K. L24 ; SHERMAN, E. A; SILBERSTEIN, L. E14 15 ; SIX, E7 8 ; TOUZOT, F1 2 4 8 ; TSYTSYKOVA, A14 15 ; XU-BAYFORD, J18 ; BERRY, C. C20 ; BAUM, C; BUSHMAN, F. D; FISCHER, A10 2 7 8 ; KOHN, D. B23 24 ; FILIPOVICH, A. H21 ; NOTARANGELO, L. D12 14 17 ; CAVAZZANA, M1 4 7 8 ; WILLIAMS, D. A11 13 14 ; THRASHER, A. J18 19 ; BLANCHE, S2 ; BLEESING, J21 ; BLONDEAU, J1 4 7 8 ; DE BOER, H; BUCKLAND, K. F19
[1] Department of Biotherapy, Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France
[2] Department of Immunology and Pediatric Hematology, Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France
[3] Centre d'Étude des Deficits Immunitaires, Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France
[4] Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, AP-HP, INSERM, Paris, France
[5] Unité de Technologies Chimiques et Biologiques pour la Santé, Centre National de la Recherche Scientifique, 8258-INSERM Unité 1022, Faculté des Sciences Pharmaceutiques et Biologiques, Université Paris Descartes, Paris, France
[6] Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, AP-HP, Le Kremlin-Bicêtre, Paris, France
[7] Imagine Institute, Paris Descartes-Sorbonne Paris Cité University, Paris, France
[8] INSERM Unités Mixtes de Recherche 1163, Laboratory of Human Lymphohematopoiesis, Paris, France
[9] Groupe Immunoscope, Immunology Department, Institut Pasteur, Paris, France
[10] College de France, Paris, France
[11] Division of Hematology-Oncology, Boston Children's Hospital, Boston, United States
[12] Division of Immunology, Boston Children's Hospital, Boston, United States
[13] Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, United States
[14] Harvard Medical School, Boston, United States
[15] Center for Human Cell Therapy, Program in Cellular and Molecular Medicine, Boston Children's Hospital, Boston, United States
[16] Division of Hematologic Malignancies, Dana-Farber Cancer Institute, Boston, United States
[17] Manton Center for Orphan Disease Research, Boston, United States
[18] Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom
[19] Section of Molecular and Cellular Immunology, University College London Institute of Child Health, London, United Kingdom
[20] Division of Biostatistics and BioInformatics, Department of Family and Preventive Medicine, University of California at San Diego, La Jolla, United States
[21] Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, United States
[22] Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, United States
[23] Department of Pediatrics, Children's Discovery and Innovation Institute, UCLA Mattel Children's Hospital, United States
[24] Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, Los Angeles, United States
[25] University of Illinois College of Medicine at Peoria, Peoria, United States
Source

The New England journal of medicine. 2014, Vol 371, Num 15, pp 1407-1417, 11 p ; ref : 37 ref

CODEN
NEJMAG
ISSN
0028-4793
Scientific domain
General medicine general surgery
Publisher
Massachusetts Medical Society, Waltham, MA
Publication country
United States
Document type
Article
Language
English
Keyword (fr)
Immunodéficit combiné sévère Médecine Vecteur Immunopathologie
Keyword (en)
Severe combined immunodeficiency Medicine Vector Immunopathology
Keyword (es)
Inmunodeficiencia combinada grave Medicina Vector Inmunopatología
Classification
Pascal
002 Biological and medical sciences / 002B Medical sciences / 002B01 General aspects

Discipline
Generalities in medical sciences
Origin
Inist-CNRS
Database
PASCAL
INIST identifier
29069609

Sauf mention contraire ci-dessus, le contenu de cette notice bibliographique peut être utilisé dans le cadre d’une licence CC BY 4.0 Inist-CNRS / Unless otherwise stated above, the content of this bibliographic record may be used under a CC BY 4.0 licence by Inist-CNRS / A menos que se haya señalado antes, el contenido de este registro bibliográfico puede ser utilizado al amparo de una licencia CC BY 4.0 Inist-CNRS

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