Toward a Functional Definition of a Rare Disease for Regulatory Authorities and Funding Agencies
- Author
- CLARKE, Joe T. R1 ; COYLE, Doug2 ; EVANS, Gerald3 ; MARTIN, Janet4 5 ; WINQUIST, Eric4 5
[1] Hospital for Sick Children and University of Toronto, Toronto, ON, Canada
[2] University of Ottawa, Ottawa, ON, Canada
[3] Kingston General Hospital and School of Medicine, Queen's University, Kingston, ON, Canada
[4] Schulich School of Medicine & Dentistry, Western University, London, ON, Canada
[5] London Health Sciences Centre, London, ON, Canada - Source
Value in health. 2014, Vol 17, Num 8, pp 757-761, 5 p ; ref : 31 ref
- ISSN
- 1098-3015
- Scientific domain
- Hygiene and public health, epidemiology, occupational medicine; Pharmacology drugs
- Publisher
- Elsevier, New York, NY
- Publication country
- United States
- Document type
- Article
- Language
- English
- Author keyword
- drug development drug reimbursement orphan drugs rare disease
- Keyword (fr)
- Autorité Définition Financement Médicament orphelin Organisme Recherche clinique Santé publique Maladie rare Remboursement
- Keyword (en)
- Authority Definition Financing Orphan drug Organism Clinical research Public health Rare disease
- Keyword (es)
- Autoridad Definición Financiación Medicamento huérfano Organismo Investigación clínica Salud pública Enfermedad rara
- Classification
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B30 Public health. Hygiene-occupational medicine / 002B30A Public health. Hygiene / 002B30A01 General aspects / 002B30A01C Planification. Prevention (methods). Intervention. Evaluation
- Pascal
- 002 Biological and medical sciences / 002B Medical sciences / 002B30 Public health. Hygiene-occupational medicine / 002B30A Public health. Hygiene / 002B30A11 Miscellaneous
- Discipline
- Public health. Hygiene-occupational medicine
- Origin
- Inist-CNRS
- Database
- PASCAL
- INIST identifier
- 29094233
Sauf mention contraire ci-dessus, le contenu de cette notice bibliographique peut être utilisé dans le cadre d’une licence CC BY 4.0 Inist-CNRS / Unless otherwise stated above, the content of this bibliographic record may be used under a CC BY 4.0 licence by Inist-CNRS / A menos que se haya señalado antes, el contenido de este registro bibliográfico puede ser utilizado al amparo de una licencia CC BY 4.0 Inist-CNRS
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DOI
10.1016/j.jval.2014.08.2672 
https://dx.doi.org/10.1016/j.jval.2014.08.2672
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