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Aspartoacylase gene transfer to the mammalian central nervous system with therapeutic implications for Canavan diseaseLEONE, P; JANSON, C. G; MCPHEE, S. W et al.Annals of neurology. 2000, Vol 48, Num 1, pp 27-38, issn 0364-5134Article

Multi-site partitioned delivery of human tyrosine hydroxylase gene with phenotypic recovery in Parkinsonian ratsLEONE, P; MCPHEE, S. W. J; JANSON, C. G et al.Neuroreport (Oxford). 2000, Vol 11, Num 6, pp 1145-1151, issn 0959-4965Article

Natural history of canavan disease revealed by proton magnetic resonance spectroscopy (1H-MRS) and diffusion-weighted MRIJANSON, C. G; MCPHEE, S. W. J; LEONE, P et al.Neuropediatrics. 2006, Vol 37, Num 4, pp 209-221, issn 0174-304X, 13 p.Article

Effects of AAV-2-mediated aspartoacylase gene transfer in the tremor rat model of Canavan diseaseMCPHEE, S. W. J; FRANCIS, J; JANSON, C. G et al.Molecular brain research. 2005, Vol 135, Num 1-2, pp 112-121, issn 0169-328X, 10 p.Article

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