Electrophysiological Phenotypes of MeCP2 A140V Mutant Mouse ModelMA, Lu-Yao; CHEN WU; JIE WU et al.CNS neuroscience & therapeutics (Print). 2014, Vol 20, Num 5, pp 420-428, issn 1755-5930, 9 p.Article

A Generalized Tip-Membrane Contact Detection Algorithm for Automated Single Cell Electroporation Using Statistical Process ControlSAKAKI, Kelly; ESMAEILSABZALI, Hadi; DECHEV, Nikolai et al.IEEE transactions on automation science and engineering. 2012, Vol 9, Num 2, pp 226-236, issn 1545-5955, 11 p.Article

AAV vectors transduce hepatocytes in vivo as efficiently in cirrhotic as in healthy rat liversSOBREVALS, L; ENGUITA, M; RODRIGUEZ, C et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 4, pp 411-417, issn 0969-7128, 7 p.Article

Benzoate X receptor zinc-finger gene switches for drug-inducible regulation of transcriptionSCHWIMMER, L. J; GONZALEZ, B; BARBAS, C. F et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 4, pp 458-462, issn 0969-7128, 5 p.Article

Complete Eradication of Xenograft Hepatoma by Oncolytic Adenovirus ZD55 Harboring TRAIL-IETD-Smac Gene with Broad Antitumor EffectWANG, Shi-Bing; YUAN TAN; WEN LEI et al.Human gene therapy. 2012, Vol 23, Num 9, pp 992-1002, issn 1043-0342, 11 p.Article

Corticospinal tract transduction: a comparison of seven adeno-associated viral vector serotypes and a non-integrating lentiviral vectorHUTSON, T. H; VERHAAGEN, J; YANEZ-MUNOZ, R. J et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 1, pp 49-60, issn 0969-7128, 12 p.Article

Critical Variables affecting clinical-grade production of the self-inactivating gamma-retroviral vector for the treatment of X-linked severe combined immunodeficiencyDER LOO, Jcm Van; SWANEY, W. P; WILLIAMS, D. A et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 8, pp 872-876, issn 0969-7128, 5 p.Article

Decreasing Disease Severity in Symptomatic, Smn^―/―;SMN2^+/+, Spinal Muscular Atrophy Mice Following scAAV9-SMN DeliveryGLASCOCK, Jacqueline J; OSMAN, Erkan Y; WETZ, Mary J et al.Human gene therapy. 2012, Vol 23, Num 3, pp 330-335, issn 1043-0342, 6 p.Article

Dynamics of melanoma tumor therapy with vesicular stomatitis virus: explaining the variability in outcomes using mathematical modelingROMMELFANGER, D. M; OFFORD, C. P; DEV, J et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 5, pp 543-549, issn 0969-7128, 7 p.Article

Effect of Helper Lipids on the Interaction of DNA with Cationic Lipid Monolayers Studied by Specular Neutron ReflectionDABKOWSKA, A. P; BARLOW, D. J; CAMPBELL, R. A et al.Biomacromolecules. 2012, Vol 13, Num 8, pp 2391-2401, issn 1525-7797, 11 p.Article

Enhanced gene delivery to the neonatal retina through systemic administration of tyrosine-mutated AAV9 : Gene Therapy for Eye DiseasesDALKARA, D; BYRNE, L. C; LEE, T et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 2, pp 176-181, issn 0969-7128, 6 p.Article

Gene-based therapies for dominantly inherited retinopathies : Gene Therapy for Eye DiseasesFARRAR, G. J; MILLINGTON-WARD, S; CHADDERTON, N et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 2, pp 137-144, issn 0969-7128, 8 p.Article

Hepatic Gene Transfer in Neonatal Mice by Adeno-Associated Virus Serotype 8 VectorLILI WANG; HUAN WANG; BELL, Peter et al.Human gene therapy. 2012, Vol 23, Num 5, pp 533-539, issn 1043-0342, 7 p.Article

Immunodominant Liver-Specific Expression Suppresses Transgene-Directed Immune Responses in Murine Pompe DiseasePING ZHANG; BAODONG SUN; OSADA, Takuya et al.Human gene therapy. 2012, Vol 23, Num 5, pp 460-472, issn 1043-0342, 13 p.Article

In Vivo Gene Transfer Strategies to Achieve Partial Correction of von Willebrand DiseaseLAN WANG; ROSENBERG, Jonathan B; DE, Bishnu P et al.Human gene therapy. 2012, Vol 23, Num 6, pp 576-588, issn 1043-0342, 13 p.Article

Inhibition of Autophagy Enhances the Effects of E1A-Defective Oncolytic Adenovirus d/922―947 Against Glioma Cells In Vitro and In VivoBOTTA, Ginevra; PASSARO, Carmela; LIBERTINI, Silvana et al.Human gene therapy. 2012, Vol 23, Num 6, pp 623-634, issn 1043-0342, 12 p.Article

Interleukin-10 expression induced by adeno-associated virus vector suppresses proteinuria in Zucker obese ratsOGURA, M; URABE, M; KUSANO, E et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 5, pp 476-482, issn 0969-7128, 7 p.Article

Intradermal DNA Vaccination Enhanced by Low-Current Electroporation Improves Antigen Expression and Induces Robust Cellular and Humoral Immune ResponsesHUTNICK, Natalie A; MYLES, Devin J. F; FERRARO, Bernadette et al.Human gene therapy. 2012, Vol 23, Num 9, pp 943-950, issn 1043-0342, 8 p.Article

Long-Term Preservation of Cardiac Structure and Function After Adeno-Associated Virus Serotype 9-Mediated Microdystrophin Gene Transfer in mdx MiceSCHINKEL, Stefanie; BAUER, Ralf; BEKEREDJIAN, Raffi et al.Human gene therapy. 2012, Vol 23, Num 6, pp 566-575, issn 1043-0342, 10 p.Article

Long-term safety of intramuscular gene transfer of non-viral FGF1 for peripheral artery diseaseNIEBUHR, A; HENRY, T; GOLDMAN, J et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 3, pp 264-270, issn 0969-7128, 7 p.Article

MicroRNAs in Genetic Disease: Rethinking the Dosage : The Therapeutic Sound of Silencing: Managing the Expectations on Targeting RNAiHENRION-CAUDE, Alexandra; GIRARD, Muriel; AMIEL, Jeanne et al.Current gene therapy. 2012, Vol 12, Num 4, pp 292-300, issn 1566-5232, 9 p.Article

Nonviral gene delivery of erythropoietin by mesenchymal stromal cellsSCHEIBE, F; GLADOW, N; MERGENTHALER, P et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 5, pp 550-560, issn 0969-7128, 11 p.Article

Prednisolone Treatment Does Not Interfere with 2-'-O-Methyl Phosphorothioate Antisense-Mediated Exon Skipping in Duchenne Muscular DystrophyVERHAART, Ingrid E. C; HEEMSKERK, Hans; KARNAOUKH, Tatyana G et al.Human gene therapy. 2012, Vol 23, Num 3, pp 262-273, issn 1043-0342, 12 p.Article

Restoration of normal BMP signaling levels and osteogenic differentiation in FOP mesenchymal progenitor cells by mutant allele-specific targetingKAPLAN, J; KAPLAN, F. S; SHORE, E. M et al.Gene therapy (Basingstoke). 2012, Vol 19, Num 7, pp 786-790, issn 0969-7128, 5 p.Article

Reversal of Metabolic and Neurological Symptoms of Phenylketonuric Mice Treated with a PAH Containing Helper-Dependent Adenoviral VectorCERRETO, Monica; MEHDAWY, Bisan; OMBRONE, Daniela et al.Current gene therapy. 2012, Vol 12, Num 1, pp 48-56, issn 1566-5232, 9 p.Article